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Neurogene Inc Is A Clinical-Stage Biotechnology Company Committed To Overcoming The Limitations Of Neurological Diseases Into Treatable Conditions, By Harnessing Its Proprietary Transgene Regulation Technology, Exact(Expression Attenuation Via Construct Tuning). It Is Building A Differentiated Product Portfolio Of Genetic Medicines For Rare Neurological Diseases With High Unmet Needs. The Drug Candidates In The Company'S Product Pipeline Include Ngn-401, Which Is In Development For The Treatment Of Rett Syndrome, Using Its Exact Platform, And Ngn-101, A Non-Exact, Conventional Gene Therapy Development Candidate For The Treatment Of Cln5 Batten Disease, Designed To Deliver The Cln5 Gene And Packaged In An Aav9 Capsid.